The promise of gene therapy looms large for families dealing with rare, genetic disorders. Such treatments…
Gene therapy
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate
Robin Alderman faces an agonizing reality: Gene therapy might cure her son Camden’s rare, inherited immune…
A rural Ugandan community is a hot spot for sickle cell disease. But one patient gives hope
MBALE, Uganda — Barbara Nabulo was one of three girls in her family. But when a…